Gene therapy for the treatment of Parkinson's disease: the nature of the biologics expands the future indications.

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Published in Pharmaceuticals (Basel) on June 04, 2012

Authors

Massimo S Fiandaca1, Krystof S Bankiewicz, Howard J Federoff

Author Affiliations

1: Translational NeuroTherapy Center, Department of Neurological Surgery, University of California San Francisco, 1855 Folsom Street, Mission Center Building, San Francisco, CA 94103, USA. Massimo.Fiandaca@ucsf.edu.

Associated clinical trials:

Safety and Efficacy of CERE-120 in Subjects With Parkinson's Disease | NCT00985517

Double-Blind, Multicenter, Sham Surgery Controlled Study of CERE-120 in Subjects With Idiopathic Parkinson's Disease | NCT00400634

Safety of CERE-120 (AAV2-NTN) in Subjects With Idiopathic Parkinson's Disease | NCT00252850

Phase I/II Study of the Safety, Efficacy and Dose Evaluation of ProSavin for the Treatment of Bilateral Idiopathic Parkinson's Disease | NCT00627588

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