One Year of Enzyme Replacement Therapy Reduces Globotriaosylceramide Inclusions in Podocytes in Male Adult Patients with Fabry Disease.

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🔗 View Article (PMID 27081853)

Published in PLoS One on April 15, 2016

Authors

Behzad Najafian1, Camilla Tøndel2,3, Einar Svarstad2,4, Alexey Sokolovkiy1, Kelly Smith1, Michael Mauer5

Author Affiliations

1: Department of Pathology, University of Washington, Seattle, United States of America.
2: Department of Clinical Medicine, University of Bergen, Bergen, Norway.
3: Department of Pediatrics, Haukeland University Hospital, Bergen, Norway.
4: Department of Medicine, Haukeland University Hospital, Bergen, Norway.
5: Departments of Pediatrics and Medicine, University of Minnesota, Minneapolis, United States of America.

Associated clinical trials:

Podocyturia - Predictor of Renal Dysfunction in Fabry Nephropathy | NCT02994303

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