Longitudinal Studies of Brain Structure and Function in MPS Disorders

Clinical Trial ID NCT01870375

PubWeight™ 9.73‹?›

🔗 Visit the ClinicalTrials.gov page for NCT01870375

Top papers

Rank Title Journal Year PubWeight™‹?›
1 Long-term outcome of Hurler syndrome patients after hematopoietic cell transplantation: an international multicenter study. Blood 2015 1.78
2 Cognitive, medical, and neuroimaging characteristics of attenuated mucopolysaccharidosis type II. Mol Genet Metab 2014 0.88
3 Neurocognition across the spectrum of mucopolysaccharidosis type I: Age, severity, and treatment. Mol Genet Metab 2015 0.87
4 Unexpected coronary artery findings in mucopolysaccharidosis. Report of four cases and literature review. Cardiovasc Pathol 2014 0.82
5 Biomarkers of bone remodeling in children with mucopolysaccharidosis types I, II, and VI. J Pediatr Rehabil Med 2014 0.81
6 Effect of recombinant human growth hormone on changes in height, bone mineral density, and body composition over 1-2 years in children with Hurler or Hunter syndrome. Mol Genet Metab 2013 0.81
7 Gene therapy for neurologic manifestations of mucopolysaccharidoses. Expert Opin Drug Deliv 2014 0.79
8 Long-Term Cognitive and Functional Outcomes in Children with Mucopolysaccharidosis (MPS)-IH (Hurler Syndrome) Treated with Hematopoietic Cell Transplantation. JIMD Rep 2016 0.78
9 Mucopolysaccharidosis (MPS) Physical Symptom Score: Development, Reliability, and Validity. JIMD Rep 2015 0.78
10 Pilot study of the safety and effect of adalimumab on pain, physical function, and musculoskeletal disease in mucopolysaccharidosis types I and II. Mol Genet Metab Rep 2017 0.77
11 Standardization of α-L-iduronidase enzyme assay with Michaelis-Menten kinetics. Mol Genet Metab 2013 0.77
12 A longitudinal study of emotional adjustment, quality of life and adaptive function in attenuated MPS II. Mol Genet Metab Rep 2016 0.76
13 Isokinetic muscle strength differences in patients with mucopolysaccharidosis I, II, and VI. J Pediatr Rehabil Med 2014 0.75
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