| Rank | Title | Journal | Year | PubWeight™‹?› |
|---|---|---|---|---|
| 1 | Design of tissue-specific regulatory cassettes for high-level rAAV-mediated expression in skeletal and cardiac muscle. | Mol Ther | 2007 | 1.65 |
| 2 | Successful regional delivery and long-term expression of a dystrophin gene in canine muscular dystrophy: a preclinical model for human therapies. | Mol Ther | 2012 | 1.13 |
| 3 | Functional capacity of dystrophins carrying deletions in the N-terminal actin-binding domain. | Hum Mol Genet | 2007 | 1.04 |
| 4 | Biodistribution and safety profile of recombinant adeno-associated virus serotype 6 vectors following intravenous delivery. | J Virol | 2008 | 0.83 |