Significantly increased lifespan and improved behavioral performances by rAAV gene delivery in adult mucopolysaccharidosis IIIB mice.

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🔗 View Article (PMID 17460717)

Published in Gene Ther on April 26, 2007

Authors

H Fu1, L Kang, J S Jennings, S S Moy, A Perez, J Dirosario, D M McCarty, J Muenzer

Author Affiliations

1: Center for Gene Therapy, Columbus Children's Research Institute, Columbus, OH 43205, USA. fuh@ccri.net

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