Becker muscular dystrophy patients with deletions around exon 51; a promising outlook for exon skipping therapy in Duchenne patients.

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Published in Neuromuscul Disord on February 13, 2010

Authors

A T J M Helderman-van den Enden1, C S M Straathof, A Aartsma-Rus, J T den Dunnen, B M Verbist, E Bakker, J J G M Verschuuren, H B Ginjaar

Author Affiliations

1: Center for Human and Clinical Genetics, The Leiden University Medical Center, Einthovenweg 20, 2333 ZC Leiden, The Netherlands. Helderman@lumc.nl

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