Evaluation of safety and pharmacokinetics of sodium 2,2 dimethylbutyrate, a novel short chain fatty acid derivative, in a phase 1, double-blind, placebo-controlled, single-dose, and repeat-dose studies in healthy volunteers.

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🔗 View Article (PMC 3904788)

Published in J Clin Pharmacol on March 21, 2011

Authors

Susan P Perrine1, William A Wargin, Michael S Boosalis, Wayne J Wallis, Sally Case, Jeffrey R Keefer, Douglas V Faller, William C Welch, Ronald J Berenson

Author Affiliations

1: HemaQuest Pharmaceuticals, Inc, Boston, MA 02110, USA. sperrine@hemaquest.com

Associated clinical trials:

Study of SDMB (2,2 Dimethylbutyrate, Sodium Salt) in Beta Thalassemia Intermedia in Thailand (ST20-P2T) | NCT01609595

Trial of HQK-1001 in Beta Thalassemia Intermedia in Lebanon (LB-04-THAL) | NCT01642758

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