Safety and liver transduction efficacy of rAAV5-cohPBGD in nonhuman primates: a potential therapy for acute intermittent porphyria.

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Published in Hum Gene Ther on December 01, 2013

Authors

Astrid Pañeda1, Esperanza Lopez-Franco, Christine Kaeppel, Carmen Unzu, Ana Gloria Gil-Royo, Delia D'Avola, Stuart G Beattie, Cristina Olagüe, Roberto Ferrero, Ana Sampedro, Itsaso Mauleon, Stephan Hermening, Florence Salmon, Alberto Benito, Juan Jose Gavira, María Eugenia Cornet, María del Mar Municio, Christof von Kalle, Harald Petry, Jesus Prieto, Manfred Schmidt, Antonio Fontanellas, Gloria González-Aseguinolaza

Author Affiliations

1: 1 Division of Hepatology and Gene Therapy, Center for Applied Medical Research , 31008 Pamplona, Spain .

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