Deleterious mutation in FDX1L gene is associated with a novel mitochondrial muscle myopathy.

PubWeight™: 0.92‹?›

🔗 View Article (PMC 4060119)

Published in Eur J Hum Genet on November 27, 2013

Authors

Ronen Spiegel1, Ann Saada2, Jonatan Halvardson3, Devorah Soiferman2, Avraham Shaag2, Simon Edvardson2, Yoseph Horovitz4, Morad Khayat5, Stavit A Shalev5, Lars Feuk3, Orly Elpeleg2

Author Affiliations

1: 1] Department of Pediatric A', Emek Medical Center, Afula, Rappaport School of Medicine, Technion, Haifa, Israel [2] Genetic Institute, Emek Medical Center, Afula, Rappaport School of Medicine, Technion, Haifa, Israel.
2: Monique and Jacques Roboh Department of Genetic Research, Hadassah, Hebrew University Medical Center, Jerusalem, Israel.
3: Department of Immunology, Genetics and Pathology, Science for Life Laboratory Uppsala, Rudbeck Laboratory, Uppsala University, Uppsala, Sweden.
4: Department of Pediatric A', Emek Medical Center, Afula, Rappaport School of Medicine, Technion, Haifa, Israel.
5: Genetic Institute, Emek Medical Center, Afula, Rappaport School of Medicine, Technion, Haifa, Israel.

Articles cited by this

A method and server for predicting damaging missense mutations. Nat Methods (2010) 78.53

dbSNP: the NCBI database of genetic variation. Nucleic Acids Res (2001) 76.97

ANNOVAR: functional annotation of genetic variants from high-throughput sequencing data. Nucleic Acids Res (2010) 43.51

MutationTaster evaluates disease-causing potential of sequence alterations. Nat Methods (2010) 16.61

The mechanism of eukaryotic translation initiation and principles of its regulation. Nat Rev Mol Cell Biol (2010) 11.19

Pushing the limits of the scanning mechanism for initiation of translation. Gene (2002) 6.47

FGF-21 as a biomarker for muscle-manifesting mitochondrial respiratory chain deficiencies: a diagnostic study. Lancet Neurol (2011) 2.36

Splice mutation in the iron-sulfur cluster scaffold protein ISCU causes myopathy with exercise intolerance. Am J Hum Genet (2008) 1.84

Formation and properties of [4Fe-4S] clusters on the IscU scaffold protein. Biochemistry (2007) 1.76

Mutations in iron-sulfur cluster scaffold genes NFU1 and BOLA3 cause a fatal deficiency of multiple respiratory chain and 2-oxoacid dehydrogenase enzymes. Am J Hum Genet (2011) 1.70

A fatal mitochondrial disease is associated with defective NFU1 function in the maturation of a subset of mitochondrial Fe-S proteins. Am J Hum Genet (2011) 1.57

Molecular view of 43 S complex formation and start site selection in eukaryotic translation initiation. J Biol Chem (2010) 1.44

Humans possess two mitochondrial ferredoxins, Fdx1 and Fdx2, with distinct roles in steroidogenesis, heme, and Fe/S cluster biosynthesis. Proc Natl Acad Sci U S A (2010) 1.40

Evaluation of enzymatic assays and compounds affecting ATP production in mitochondrial respiratory chain complex I deficiency. Anal Biochem (2004) 1.36

Deficiency of skeletal muscle succinate dehydrogenase and aconitase. Pathophysiology of exercise in a novel human muscle oxidative defect. J Clin Invest (1991) 1.26

Biochemical assays for mitochondrial activity: assays of TCA cycle enzymes and PDHc. Methods Cell Biol (2007) 1.20

Both human ferredoxins 1 and 2 and ferredoxin reductase are important for iron-sulfur cluster biogenesis. Biochim Biophys Acta (2011) 1.03

Clinical manifestation and a new ISCU mutation in iron-sulphur cluster deficiency myopathy. Brain (2009) 1.03

Tissue-specific splicing of ISCU results in a skeletal muscle phenotype in myopathy with lactic acidosis, while complete loss of ISCU results in early embryonic death in mice. Hum Genet (2010) 0.94

Single base-pair substitutions at the translation initiation sites of human genes as a cause of inherited disease. Hum Mutat (2011) 0.92

Articles by these authors

A deleterious mutation in DNAJC6 encoding the neuronal-specific clathrin-uncoating co-chaperone auxilin, is associated with juvenile parkinsonism. PLoS One (2012) 1.20

Hereditary sensory autonomic neuropathy caused by a mutation in dystonin. Ann Neurol (2012) 1.13

Autoimmune lymphoproliferative syndrome-like disease in patients with LRBA mutation. Clin Immunol (2015) 1.04

Agenesis of corpus callosum and optic nerve hypoplasia due to mutations in SLC25A1 encoding the mitochondrial citrate transporter. J Med Genet (2013) 0.98

The 3' addition of CCA to mitochondrial tRNASer(AGY) is specifically impaired in patients with mutations in the tRNA nucleotidyl transferase TRNT1. Hum Mol Genet (2015) 0.93

Mutations in the Mitochondrial Citrate Carrier SLC25A1 are Associated with Impaired Neuromuscular Transmission. J Neuromuscul Dis (2016) 0.81

A human laterality disorder caused by a homozygous deleterious mutation in MMP21. J Med Genet (2015) 0.80

Cytokine secretion and NK cell activity in human ADAM17 deficiency. Oncotarget (2015) 0.79

Extending the clinical and immunological phenotype of human interleukin-21 receptor deficiency. Haematologica (2014) 0.79

A human laterality disorder associated with a homozygous WDR16 deletion. Eur J Hum Genet (2014) 0.78

Congenital valvular defects associated with deleterious mutations in the PLD1 gene. J Med Genet (2016) 0.77

Organic Solute Transporter-beta (SLC51B) Deficiency in Two Brothers with Congenital Diarrhea and Features of Cholestasis. Hepatology (2017) 0.75

Homozygous mutation in PTRH2 gene causes progressive sensorineural deafness and peripheral neuropathy. Am J Med Genet A (2017) 0.75

Mutation in the COX4I1 gene is associated with short stature, poor weight gain and increased chromosomal breaks, simulating Fanconi anemia. Eur J Hum Genet (2017) 0.75

Mutations in EFL1, an SBDS partner, are associated with infantile pancytopenia, exocrine pancreatic insufficiency and skeletal anomalies in a Shwachman-Diamond like syndrome. J Med Genet (2017) 0.75

Homozygous mutation, p.Pro304His, in IDH3A, encoding isocitrate dehydrogenase subunit is associated with severe encephalopathy in infancy. Neurogenetics (2017) 0.75