The LSD1 inhibitor RN-1 induces fetal hemoglobin synthesis and reduces disease pathology in sickle cell mice.

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Published in Blood on June 01, 2015

Authors

Shuaiying Cui1, Kim-Chew Lim2, Lihong Shi2, Mary Lee2, Natee Jearawiriyapaisarn2, Greggory Myers2, Andrew Campbell3, David Harro4, Shigeki Iwase5, Raymond C Trievel6, Angela Rivers7, Joseph DeSimone8, Donald Lavelle8, Yogen Saunthararajah9, James Douglas Engel2

Author Affiliations

1: Department of Cell and Developmental Biology, University of Michigan Medical School, Ann Arbor, MI;
2: Department of Cell and Developmental Biology.
3: Department of Pediatrics and Infectious Diseases.
4: Department of Pathology.
5: Department of Human Genetics, and.
6: Department of Biological Chemistry, University of Michigan, Ann Arbor, MI;
7: Jesse Brown VA Medical Center, Department of Pediatrics, and.
8: Department of Pediatrics, and Department of Medicine, University of Illinois at Chicago, Chicago, IL; and.
9: Cleveland Clinic, Cleveland, OH.

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