Published in Hum Mol Genet on April 22, 2016
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Gene therapy for muscular dystrophy: moving the field forward. Pediatr Neurol (2014) 0.91
Progress and prospects of gene therapy clinical trials for the muscular dystrophies. Hum Mol Genet (2015) 0.89
Duchenne muscular dystrophy gene therapy in the canine model. Hum Gene Ther Clin Dev (2015) 0.86
Postnatal changes in sarcolemmal organization in the mdx mouse. Neuromuscul Disord (2005) 0.85
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Characterization of 65 epitope-specific dystrophin monoclonal antibodies in canine and murine models of duchenne muscular dystrophy by immunostaining and western blot. PLoS One (2014) 0.79
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Dystrophin knockdown mice suggest that early, transient dystrophin expression might be enough to prevent later pathology. Neuromuscul Disord (2008) 0.76
Safe and bodywide muscle transduction in young adult Duchenne muscular dystrophy dogs with adeno-associated virus. Hum Mol Genet (2015) 1.16
Dystrophin contains multiple independent membrane-binding domains. Hum Mol Genet (2016) 0.75