Intrathecal enzyme replacement therapy reverses cognitive decline in mucopolysaccharidosis type I.

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🔗 View Article (PMID 28211988)

Published in Am J Med Genet A on March 01, 2017

Authors

Igor Nestrasil1, Elsa Shapiro1, Alena Svatkova1,2, Patricia Dickson3, Agnes Chen3, Amy Wakumoto1, Alia Ahmed1, Edward Stehel4, Sarah McNeil4, Curtis Gravance5, Elizabeth Maher4

Author Affiliations

1: University of Minnesota, Minneapolis, Minnesota.
2: Multimodal and Functional Neuroimaging Research Group, CEITEC-Central European Institute of Technology, Masaryk University, Brno, Czech Republic.
3: Los Angeles Biomedical Institute at Harbor-UCLA, Torrance, California.
4: University of Texas Southwestern Medical Center, Dallas, Texas.
5: Ryan Foundation, Carrollton, Texas.

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