The role of sebelipase alfa in the treatment of lysosomal acid lipase deficiency.

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Published in Therap Adv Gastroenterol on April 26, 2017

Authors

Angelika L Erwin1

Author Affiliations

1: Center for Personalized Genomic Healthcare, Genomic Medicine Institute, Cleveland Clinic, 9500 Euclid Ave, NE-50, Cleveland, OH 44195, USA.

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