Numerous transcriptional alterations in liver persist after short-term enzyme-replacement therapy in a murine model of mucopolysaccharidosis type VII.

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Published in Biochem J on April 15, 2004

Authors

Josh C Woloszynek1, Marie Roberts, Trey Coleman, Carole Vogler, William Sly, Clay F Semenkovich, Mark S Sands

Author Affiliations

1: Department of Medicine, Washington University School of Medicine, St. Louis, MO 63110, USA.

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