Improved outcome of N-butyldeoxygalactonojirimycin-mediated substrate reduction therapy in a mouse model of Sandhoff disease.

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Published in Neurobiol Dis on August 01, 2004

Authors

Ulrika Andersson1, David Smith, Mylvaganam Jeyakumar, Terry D Butters, Mario Cortina Borja, Raymond A Dwek, Frances M Platt

Author Affiliations

1: Department of Biochemistry, Glycobiology Institute, University of Oxford, Oxford OX1 3QU, UK.

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