Long-term efficacy and safety of mipomersen in patients with familial hypercholesterolaemia: 2-year interim results of an open-label extension.

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🔗 View Article (PMC 4344956)

Published in Eur Heart J on December 23, 2013

Authors

Raul D Santos1, P Barton Duell2, Cara East3, John R Guyton4, Patrick M Moriarty5, Wai Chin6, Robert S Mittleman6

Author Affiliations

1: Heart Institute (InCor) University of Sao Paulo Medical School Hospital, Sao Paulo, Brazil raul.santos@incor.usp.br rdsf@uol.com.br.
2: Oregon Health and Science University, Portland, OR, USA.
3: Soltero Cardiovascular Research Center Baylor University Medical Center, Dallas, TX, USA.
4: Duke University Medical Center, Durham, NC, USA.
5: Kansas University Atherosclerosis & LDL-Apheresis Center, Kansas City, KS, USA.
6: Genzyme Corporation, Cambridge, MA, USA.

Associated clinical trials:

Study to Assess the Safety and Efficacy of ISIS 301012 (Mipomersen) in Homozygous Familial Hypercholesterolemia (RADICHOL 1) | NCT00607373

Efficacy and Safety Study of ISIS 301012 (Mipomersen) as Add-on in Familial Hypercholesterolemic Patients With Coronary Artery Disease (RADICHOL II) | NCT00706849

Safety and Efficacy of Mipomersen in Patients With Severe Hypercholesterolemia on a Maximally Tolerated Lipid-Lowering Regimen and Who Are Not on Apheresis | NCT00794664

An Open-label Extension Study to Assess the Long-term Safety and Efficacy of ISIS 301012 (Mipomersen) in Patients With Familial Hypercholesterolemia or Severe-Hypercholesterolemia | NCT00694109

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