Towards a cure for Fibrodysplasia ossificans progressiva.

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🔗 View Article (PMID 27867996)

Published in Ann Transl Med on October 01, 2016

Authors

Gonzalo Sanchez-Duffhues1, David J J de Gorter2, Peter Ten Dijke1

Author Affiliations

1: Department of Molecular Cell Biology and Cancer Genomics Centre Netherlands, Leiden University Medical Centre, Leiden, The Netherlands.
2: Institute of Experimental Musculoskeletal Medicine, University Hospital Münster, Münster, Germany.

Associated clinical trials:

An Open-Label Extension Study of Palovarotene to Treat Preosseous Flare-ups in FOP Subjects | NCT02279095

In-Home Evaluation of Episodic Administration of Palovarotene in Fibrodysplasia Ossificans Progressiva (FOP) Subjects | NCT02521792

A Study to Examine the Safety and Tolerability of Single Ascending Doses of REGN2477 | NCT02870400

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