Complete correction of hemophilia A with adeno-associated viral vectors containing a full-size expression cassette.

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Published in Hum Gene Ther on June 01, 2008

Authors

Hui Lu1, Lingxia Chen, Jinhui Wang, Bernd Huack, Rita Sarkar, Shangzhen Zhou, Ray Xu, Qiulan Ding, Xuefeng Wang, Hongli Wang, Weidong Xiao

Author Affiliations

1: Department of Pediatrics, University of Pennsylvania Medical Center and Children's Hospital of Philadelphia, Philadelphia, PA 19104, USA.

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