Widespread spinal cord transduction by intrathecal injection of rAAV delivers efficacious RNAi therapy for amyotrophic lateral sclerosis.

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Published in Hum Mol Genet on September 18, 2013

Authors

Hongyan Wang1, Bin Yang, Linghua Qiu, Chunxing Yang, Joshua Kramer, Qin Su, Yansu Guo, Robert H Brown, Guangping Gao, Zuoshang Xu

Author Affiliations

1: Department of Biochemistry and Molecular Pharmacology.

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