RNA toxicity from the ALS/FTD C9ORF72 expansion is mitigated by antisense intervention.

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Published in Neuron on October 16, 2013

Authors

Christopher J Donnelly1, Ping-Wu Zhang, Jacqueline T Pham, Aaron R Haeusler, Aaron R Heusler, Nipun A Mistry, Svetlana Vidensky, Elizabeth L Daley, Erin M Poth, Benjamin Hoover, Daniel M Fines, Nicholas Maragakis, Pentti J Tienari, Leonard Petrucelli, Bryan J Traynor, Jiou Wang, Frank Rigo, C Frank Bennett, Seth Blackshaw, Rita Sattler, Jeffrey D Rothstein

Author Affiliations

1: Department of Neurology, Johns Hopkins University, 855 N Wolfe Street, Rangos 2-270, Baltimore, MD 21205, USA; Brain Science Institute, Johns Hopkins University, 855 N Wolfe Street, Rangos 2-270, Baltimore, MD 21205, USA.

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