Collaborative development of 2-hydroxypropyl-β-cyclodextrin for the treatment of Niemann-Pick type C1 disease.

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Published in Curr Top Med Chem on January 01, 2014

Authors

Elizabeth A Ottinger, Mark L Kao, Nuria Carrillo-Carrasco, Nicole Yanjanin, Roopa Kanakatti Shankar, Marjo Janssen, Marcus Brewster, Ilona Scott, Xin Xu, Jim Cradock, Pramod Terse, Seameen J Dehdashti, Juan Marugan, Wei Zheng, Lili Portilla, Alan Hubbs, William J Pavan, John Heiss, Charles H Vite, Steven U Walkley, Daniel S Ory, Steven A Silber, Forbes D Porter, Christopher P Austin, John C McKew1

Author Affiliations

1: Division of PreClinical Innovation, National Center for Advancing Translational Sciences (NCATS), National Institutes of Health, MSC 3370, Rockville, MD 20850, United States. ottingerea@mail.nih.gov.

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