Glucocerebrosidase 2 gene deletion rescues type 1 Gaucher disease.

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Published in Proc Natl Acad Sci U S A on March 17, 2014

Authors

Pramod K Mistry1, Jun Liu, Li Sun, Wei-Lien Chuang, Tony Yuen, Ruhua Yang, Ping Lu, Kate Zhang, Jianhua Li, Joan Keutzer, Agnes Stachnik, Albert Mennone, James L Boyer, Dhanpat Jain, Roscoe O Brady, Maria I New, Mone Zaidi

Author Affiliations

1: Department of Medicine, Yale School of Medicine, New Haven, CT 06520.

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