Hyperactive sleeping beauty transposase enables persistent phenotypic correction in mice and a canine model for hemophilia B.

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Published in Mol Ther on August 17, 2010

Authors

Martin A Hausl1, Wenli Zhang, Nadine Müther, Christina Rauschhuber, Helen G Franck, Elizabeth P Merricks, Timothy C Nichols, Mark A Kay, Anja Ehrhardt

Author Affiliations

1: Max von Pettenkofer-Institut, Department of Virology, Ludwig-Maximilians-Universität Munich, Munich, Germany.

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