Pip5 transduction peptides direct high efficiency oligonucleotide-mediated dystrophin exon skipping in heart and phenotypic correction in mdx mice.

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Published in Mol Ther on April 19, 2011

Authors

HaiFang Yin1, Amer F Saleh, Corinne Betts, Patrizia Camelliti, Yiqi Seow, Shirin Ashraf, Andrey Arzumanov, Suzan Hammond, Thomas Merritt, Michael J Gait, Matthew Ja Wood

Author Affiliations

1: Department of Physiology, Anatomy and Genetics, University of Oxford, Oxford, UK.

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