Published in Dis Model Mech on March 01, 2015
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The emerging role of viral vectors as vehicles for DMD gene editing. Genome Med (2016) 0.76
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Gait characterization in golden retriever muscular dystrophy dogs using linear discriminant analysis. BMC Musculoskelet Disord (2017) 0.75
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GRMD cardiac and skeletal muscle metabolism gene profiles are distinct. BMC Med Genomics (2017) 0.75
Adenoviral vectors encoding CRISPR/Cas9 multiplexes rescue dystrophin synthesis in unselected populations of DMD muscle cells. Sci Rep (2016) 0.75
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Early loss of ambulation is not a representative clinical feature in Duchenne muscular dystrophy dogs: remarks on the article of Barthélémy et al. Dis Model Mech (2015) 0.75
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Muscular dystrophy in a dish: engineered human skeletal muscle mimetics for disease modeling and drug discovery. Drug Discov Today (2016) 0.75
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Nanotherapy for Duchenne muscular dystrophy. Wiley Interdiscip Rev Nanomed Nanobiotechnol (2017) 0.75
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