Antisense oligonucleotide treatment ameliorates alpha-1 antitrypsin-related liver disease in mice.

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Published in J Clin Invest on December 20, 2013

Authors

Shuling Guo, Sheri L Booten, Mariam Aghajan, Gene Hung, Chenguang Zhao, Keith Blomenkamp, Danielle Gattis, Andrew Watt, Susan M Freier, Jeffery H Teckman, Michael L McCaleb, Brett P Monia

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