Adenoviral vectors encoding CRISPR/Cas9 multiplexes rescue dystrophin synthesis in unselected populations of DMD muscle cells.

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🔗 View Article (PMID 27845387)

Published in Sci Rep on November 15, 2016

Authors

Ignazio Maggio1, Jin Liu1, Josephine M Janssen1, Xiaoyu Chen1, Manuel A F V Gonçalves1

Author Affiliations

1: Leiden University Medical Center, Department of Molecular Cell Biology, Einthovenweg 20, 2333 ZC, Leiden, the Netherlands.

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