Mice lacking both subunits of lysosomal beta-hexosaminidase display gangliosidosis and mucopolysaccharidosis.

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Published in Nat Genet on November 01, 1996

Authors

K Sango1, M P McDonald, J N Crawley, M L Mack, C J Tifft, E Skop, C M Starr, A Hoffmann, K Sandhoff, K Suzuki, R L Proia

Author Affiliations

1: Section on Biochemical Genetics, National Institute of Diabetes and Digestive and Kidney Diseases, National Institutes of Health, Bethesda, Maryland 20892-1810, USA.

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