In vivo delivery of human acid ceramidase via cord blood transplantation and direct injection of lentivirus as novel treatment approaches for Farber disease.

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Published in Mol Genet Metab on September 20, 2008

Authors

Shobha Ramsubir1, Takahiro Nonaka, Carmen Bedia Girbés, Stéphane Carpentier, Thierry Levade, Jeffrey A Medin

Author Affiliations

1: Department of Medical Biophysics, University of Toronto, Toronto, Ontario, Canada.

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