Published in Nucleic Acids Res on March 29, 2012
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Molecular basis of xeroderma pigmentosum group C DNA recognition by engineered meganucleases. Nature (2008) 2.37
Nanoparticles for the delivery of genes and drugs to human hepatocytes. Nat Biotechnol (2003) 2.34
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Engineered I-CreI derivatives cleaving sequences from the human XPC gene can induce highly efficient gene correction in mammalian cells. J Mol Biol (2007) 1.68
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Structural evidence for iron-free citrate and ferric citrate binding to the TonB-dependent outer membrane transporter FecA. J Mol Biol (2003) 1.63
A revised annotation and comparative analysis of Helicobacter pylori genomes. Nucleic Acids Res (2003) 1.59
Chronic systemic therapy with low-dose morpholino oligomers ameliorates the pathology and normalizes locomotor behavior in mdx mice. Mol Ther (2010) 1.48
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A diacylglycerol lipase-CB2 cannabinoid pathway regulates adult subventricular zone neurogenesis in an age-dependent manner. Mol Cell Neurosci (2008) 1.30
megaTALs: a rare-cleaving nuclease architecture for therapeutic genome engineering. Nucleic Acids Res (2013) 1.30
Structure of colicin I receptor bound to the R-domain of colicin Ia: implications for protein import. EMBO J (2007) 1.27
In vivo selection of engineered homing endonucleases using double-strand break induced homologous recombination. Nucleic Acids Res (2005) 1.26
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Codon and mRNA sequence optimization of microdystrophin transgenes improves expression and physiological outcome in dystrophic mdx mice following AAV2/8 gene transfer. Mol Ther (2008) 1.24
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Efficient in toto targeted recombination in mouse liver by meganuclease-induced double-strand break. J Gene Med (2006) 1.20
Molecular basis of engineered meganuclease targeting of the endogenous human RAG1 locus. Nucleic Acids Res (2010) 1.19
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Histidine-rich amphipathic peptide antibiotics promote efficient delivery of DNA into mammalian cells. Proc Natl Acad Sci U S A (2003) 1.13
Generation of redesigned homing endonucleases comprising DNA-binding domains derived from two different scaffolds. Nucleic Acids Res (2009) 1.13
Phenotypic correction of alpha-sarcoglycan deficiency by intra-arterial injection of a muscle-specific serotype 1 rAAV vector. Mol Ther (2007) 1.13